NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

A new gene therapy for people who can have a stem cell transplant but do not have a suitable donor has been approved.

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

The government is using sickle cell treatments to test a new strategy: paying only if the therapies benefit patients. With ...

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital. Many people with sickle ...

CHICAGO (WLS) -- Sickle cell anemia disproportionately affects Black people, causing severe pain, potential organ damage and in some cases, death. Many times, only blood transfusions can provide ...

Caring Cross, a 501(c)(3) non-profit dedicated to improving access to advanced therapies, and Boston Children's Hospital today announced a collaboration to provide a sustainable, affordable pathway ...

LOS ANGELES (KABC) -- It's been more than a month since the FDA approved two milestone gene-editing treatments for sickle cell disease, but lining up patients for these therapies will be a challenge ...

Evelyn Quartey carries the sickle cell trait, as did her ex-husband and first son, Emmanuel, who passed away from Sickle Cell Disease in 2009 at 7. Her younger son Gerald had been diagnosed with the ...

At the moment, the only remedy for sickle-cell disease is a dangerous and expensive bone marrow transplant, an option rarely used. An effective gene therapy would not be simple or inexpensive, but it ...